Human Gene Therapy

Editor-in-Chief

Terence R. Flotte, MD
Celia and Isaac Haidak Professor of Medical Education
Dean of School of Medicine
Provost and Executive Deputy Chancellor
University of Massachusetts Chan Medical School
55 Lake Avenue North
Worcester, MA, USA 01655 

Deputy Editor-in-Chief

Guangping Gao, PhD
Horae Gene Therapy Center & Department of Microbiology and Physiology Systems
University of Massachusetts Chan Medical School
368 Plantation Street, AS6-2049
Worcester, MA, USA 01605

European Editor

Hildegard Büning, PhD
Laboratory for Infection Biology & Gene Transfer
Institute of Experimental Hematology
Hannover Medical School
OE 6960, J11
Carl-Neuberg-Str. 1
30625 Hannover, Germany

Asian Editor

Yu-Quan Wei, MD, PhD
National Key Laboratory of Biotherapy and Cancer Center
West China Hospital, West China Medical
School, Sichuan University
Gaopeng Street, Keyuan Street Road 4, No. 1
Chengdu, Sichuan 610041
P.R. China

Executive Editor

Kevin Davies, PhD
Mary Ann Liebert, Inc., publishers
New Rochelle, NY, USA
 

Deputy Editors

Seng H. Cheng, PhD
Senior Vice President & Chief Scientific Officer, Rare Disease
Pfizer
Andover, MA, USA

Mark A. Kay, MD, PhD
Departments of Pediatrics and Genetics
Stanford University School of Medicine
Stanford, CA, USA

Thierry VandenDriessche, PhD
Department of Gene Therapy & Regenerative Medicine
Vrije Universiteit Brussel
    Brussels, Belgium
Department of Cardiovascular Sciences, Center for Molecular & Vascular Biology
University of Leuven
    Leuven, Belgium

Associate Editors

Jennifer Adair, PhD
Stem Cell and Gene Therapy Program
Fred Hutchinson Cancer Research Center
Seattle, WA, USA
 

Robin R. Ali, PhD, FMedSci
Centre for Cell and Gene Therapy, King’s College London
    London, United Kingdom
Kellogg Eye Center, University of Michigan
    Ann Arbor, MI, USA

K. Reed Clark, PhD
Ultragenyx Gene Therapy
Cambridge, MA, USA
 

Dongsheng Duan, PhD
Margaret Proctor Mulligan Professor in Medical Research 
University of Missouri
Columbia, MO, USA

Maria P. Limberis, PhD
Spirovant Sciences, Inc.
Philadelphia, PA, USA
 

Senior Consulting Editors

Jean Bennett, MD, PhD
Center for Advanced Retinal and Ocular Therapeutics
Department of Ophthalmology
Perelman School of Medicine
University of Pennsylvania
Philadelphia, PA, USA

J. Keith Joung, MD, PhD
Department of Pathology, Harvard Medical School
    Boston, MA, USA
Molecular Pathology Unit, Massachusetts General Hospital
    Charlestown, MA, USA
Center for Cancer Research and Center for Computational and Integrative Biology
Massachusetts General Hospital
    Charlestown, MA, USA

Carl H. June, MD
Department of Pathology and Laboratory Medicine
Center for Cellular Immunotherapy
University of Pennsylvania 
Perelman School of Medicine
Philadelphia, PA, USA

Nathalie Cartier Lacave, MD
INSERM UMR1169: Biotherapy for Neurodegenerative Diseases
CEA, Molecular Imaging Research Center 
University Paris Saclay
Paris, France 

Feng Zhang, PhD
Broad Institute of MIT and Harvard
    Cambridge, MA, USA
McGovern Institute for Brain Research
Massachusetts Institute of Technology
    Cambridge, MA, USA
Howard Hughes Medical Institute
    Cambridge, MA, USA

Scientific Editorial Board

Kari Airenne, PhD
Kuopio Center for Gene and Cell Therapy
Kuopio, Finland
 

Ramon Alemany, PhD
Institut Català d´Oncologia-IDIBELL
Barcelona, Spain
 

Ian Edward Alexander, MBBS, PhD
Sydney Children’s Hospitals Network and Children’s Medical Research Institute
Sydney, Australia
 

Daniel G. Anderson, PhD
Massachusetts Institute of Technology
Cambridge, MA, USA
 

Aravind Asokan, PhD
Duke University
Durham, NC, USA


Takis Athanasopoulos, PhD    
GlaxoSmithKline    
Brentford, United Kingdom

Ana Rita Batista, PhD
University of Massachusetts Chan Medical School
Worcester, MA, USA
 

Christopher Baum, MD, PhD
Hannover Medical School
Hannover, Germany

Janet Benson, PhD, DABAT
Lovelace Respiratory Research Institute    
Albuquerque, NM, USA

Michael R. Betts, PhD    
University of Pennsylvania Perelman School of Medicine
Philadelphia, PA, USA

Alessandra Biffi, MD
Harvard Medical School
Cambridge, MA, USA


Claire Booth, MBBS, PhD
Institute of Child Health
University College London
London, United Kingdom

Shannon E. Boye, PhD
University of Florida
Gainesville, FL, USA
 

Xandra O. Breakefield, PhD
Massachusetts General Hospital
Boston, MA, USA

Juan A. Bueren, PhD
CIEMAT
Madrid, Spain

David Bumcrot, PhD
Editas Medicine, Inc
Cambridge, MA, USA

Barry J. Byrne, MD, PhD
University of Florida College of Medicine
Gainesville, FL, USA


Roberto Calcedo, PhD
Affinia Therapeutics
Waltham, MA, USA
 

Toni Cathomen, PhD
University of Freiburg
Freiburg im Breisgau, Germany
 

Joy Cavagnaro, PhD, DABT, ATS          
Access BIO    
Somerset, NJ, USA

Saswati Chatterjee, PhD
City of Hope National Medical Center
Duarte, CA, USA
 

Nathalie Clément, PhD
Unicorn Consultations, LLC
Gainesville, FL, USA
 

Thomas J. Conlon, PhD
CR Scientific and Compliance Consulting, LLC
    Gainesville, FL, USA
Michelson Found Animals Foundation, LLC
    Los Angeles, CA, USA

Kenneth Cornetta, MD
Indiana University School of Medicine
Indianapolis, IN, USA

Larry A. Couture, PhD
Beckman Research Institute of City of Hope
Duarte, CA, USA

Gay M. Crooks, MB, BS
University of California–Los Angeles
Los Angeles, CA, USA

Pedro E. Cruz, PhD
ECBio, S.A.
Lisbon, Portugal

Ronald G. Crystal, MD
Weill Cornell Medical College
New York, NY, USA


Martin Donnelley, PhD
University of Adelaide
Adelaide, Australia

Boro Dropulic, PhD, MBA
Lentigen Corporation
Gaithersburg, MD, USA

Anja Ehrhardt, PhD
University of Munich
Munich, Germany

John F. Engelhardt, PhD
University of Iowa
Iowa City, IA, USA


Erik Falck-Pedersen, PhD
Weill Cornell Medical College
New York, NY, USA

Boris Fehse, PhD
University Medical Center
Hamburg-Eppendorf
Hamburg, Germany

Keith Foster, PhD
University of Reading
Reading, England

Maria Cristina Galli, PhD
Istituto Superiore di Sanità
Rome, Italy

Anne Galy, PhD
INSERM-Généthon
Évry, France


Charles Gersbach, PhD
Duke University
Durham, NC, USA
 

Gloria Gonzalez-Aseguinolaza, PhD
Foundation for Applied Medical
Research (FIMA), University of Navarra
Pamplona, Spain

Uta Griesenbach, PhD
Imperial College London
London, United Kingdom

Dirk Grimm, PhD
Heidelberg University
Heidelberg, Germany


Alisha M. Gruntman, DVM, PhD
University of Massachusetts Chan Medical School
    Worcester, MA, USA
Cummings School of Veterinary Medicine at Tufts University
    North Grafton, MA, USA

Kirk Hammond, MD
University of California–San Diego, and
VA San Diego Healthcare System
San Diego, CA, USA

Renzhi Han, PhD
The Ohio State University
Columbus, OH, USA
 

Akseli Hemminki, MD, PhD
University of Helsinki
Helsinki, Finland

Ulrich R. Hengge, MD
Heinrich-Heine-University
Düsseldorf, Germany

Roland W. Herzog, PhD
University of Florida
Gainesville, FL, USA

Giridhara R. Jayandharan, PhD
Indian Institute of Technology
Kanpur, India
 

Stephen M. Kaminsky, PhD
Weill Medical College of Cornell University
New York, NY, USA
 

Chang-Yuil Kang, PhD
Seoul National University
Seoul, South Korea
 

Noriyuki Kasahara, MD, PhD
University of Miami
Miami, FL, USA

Allison Keeler-Klunk, PhD
University of Massachusetts Chan Medical School
Worcester, MA, USA


Hans-Peter Kiem, MD
University of Washington School of Medicine
Seattle, WA, USA

David Klatzmann, MD, PhD
INSERM
Paris, France
 

Stefan Kochanek, MD
Ulm University
Ulm, Germany

Robert M. Kotin, PhD
University of Massachusetts Chan Medical School
    Worcester, MA, USA
Generation Bio
    Cambridge, MA, USA

Francois M. Lemoine, MD, PhD
University Pierre and Marie Curie
Paris, France

Chen Ling, PhD
Fudan University
Shanghai, China
 

Shan Lu, MD, PhD, MHA
University of Massachusetts Chan Medical School
Worcester, MA, USA
 

Morgan L. Maeder, PhD
Editas Medicine
Cambridge, MA, USA

Fulvio Mavilio, PhD
University of Modena and Reggio Emilia
Modena, Italy
 

Maritza McIntyre, PhD
REGENX Biosciences
Rockville, MD, USA

R. Scott McIvor, PhD
University of Minnesota
Minneapolis, MN, USA


Otto-Wilhelm Merten, PhD
Miltenyi Biotec
Bergisch Gladbach, Germany
 

Federico Mingozzi, PhD
Généthon
Évry, France

Hiroaki Mizukami, MD, PhD
Jichi Medical University
Tochigi-ken, Japan
 

Eugenio Montini, PhD
San Raffaele Telethon Institute for Gene Therapy
Milan Italy

Hiroyuki Nakai, MD, PhD
Oregon Health & Science University
Portland, OR, USA

Gopalan Narayanan, MD
Voisin Consulting Life Sciences
Cambridge, MA, USA

Stuart Nicklin, PhD
University of Glasgow
Glasgow, United Kingdom

Timothy O’Brien, MD, PhD
National University of Ireland, Galway
Galway, Ireland
 

Nicole K. Paulk, PhD
University of California–San Francisco
San Francisco, CA, USA


Katherine Ponder, MD
Washington University School of Medicine
St. Louis, MO, USA

Felipe Prosper, MD
University of Navarra
Pamplona, Spain


ZhiYong Qian, MD
Sichuan University
Chengdu, China


John E.J. Rasko, MBBS, PhD
Centenary Institute and Royal Prince Alfred Hospital
Camperdown, Australia


Paul D. Robbins, PhD
University of Pittsburgh School of Medicine
Pittsburgh, PA, USA

David W. Russell, MD, PhD
University of Washington
Seattle, WA, USA

Steven J. Russell, MD, PhD
Mayo Clinic College of Medicine
Rochester, MN, USA
 

Michel Sadelain, MD, PhD
Memorial Sloan Kettering Cancer Center
New York, NY, USA

Paula Salmikangas, PhD
NDA Sweden
Upplands Väsby, Sweden
 

David Schaffer, PhD
University of California–Berkeley
Berkeley, CA, USA
 

Axel Schambach, MD, PhD
Hannover Medical School
Hannover, Germany

Martin Schleef, PhD
PlasmidFactory
Bielefeld, Germany
 

Manfred Schmidt, PhD
National Center for Tumor Diseases
Heidelberg, Germany

Richard O. Snyder, PhD
Thermo Fisher Scientific
Alachua, FL, USA
 

Sihong Song, PhD
University of Florida
Gainesville, FL, USA
 

Erik J. Sontheimer, PhD
University of Massachusetts Chan Medical School
Worcester, MA, USA


Arun Srivastava, PhD
University of Florida College of Medicine
Gainesville, FL, USA
 

Renata Stripecke, PhD
Hannover Medical School
Hannover, Germany

Ryota Tamura, MD, PhD
Keio University School of Medicine
Tokyo, Japan
 

Mark Tangney, PhD
Cork Cancer Research Centre
Cork, Ireland

Victor W. van Beusechem, PhD
VU University Medical Center
Amsterdam, Netherlands

Luk H. Vandenberghe, PhD
Harvard Medical School
Cambridge, MA, USA
 

Els Verhoeyen, PhD
University of Lyon
Lyon, France


Christof von Kalle, MD, PhD
Berlin Institute of Health and
Charité Clinical Study Center
Berlin, Germany

Sam Wadsworth, PhD
Ultragenyx Pharmaceutical
Cambridge, MA, USA
 

Gerard Wagemaker, PhD
Erasmus University Medical Center
Rotterdam, Netherlands
 

Qiang Wang, PhD
University of Pennsylvania
Philadelphia, PA, USA

John H. Wolfe, VMD, PhD
University of Pennsylvania
Philadelphia, PA, USA


J. Fraser Wright, PhD
Stanford University School of Medicine
Stanford, CA, USA

Joseph C. Wu, MD, PhD
Stanford University School of Medicine
Stanford, CA, USA


Weidong Xiao, PhD
Indiana University
Indianapolis, IN, USA
 

Xiao Xiao, PhD
University of North Carolina
Chapel Hill, NC, USA

Wen Xue, PhD
University of Massachusetts Chan Medical School
Worcester, MA, USA


Rafael J. Yáñez-Muñoz, PhD
Royal Holloway, University of London
Egham, United Kingdom
 

Yiping Yang, MD, PhD
Duke University Medical Center
Durham, NC, USA

Seppo Yla-Herttuala, MD, PhD
University of Eastern Finland
Kuopio, Finland


Yoshi Yonemitsu, MD, PhD
Kyushu University
Fukuoka, Japan

Managing Editors

Thomas Gallagher, PhD
Horae Gene Therapy Center
University of Massachusetts Chan Medical School
55 Lake Ave North
Worcester, MA, USA
Thomas.Gallagher@umassmed.edu

Susan K. Jensen, BA
Mary Ann Liebert, Inc., publishers
New Rochelle, NY, USA
 

Founding Editor

W. French Anderson, MD