News Releases
Monday, January 31, 2022
Dexamethasone Enhances Transgene Expression When Administered After Gene TherapyTuesday, January 25, 2022
Gene Therapy for the Treatment of Huntington’s DiseaseThursday, December 16, 2021
Determining the Minimally Effective Dose for Gene Therapy in Hemophilia AThursday, December 10, 2020
AAV Capsid-Promoter Interactions in the Non-Human Primate BrainMonday, November 16, 2020
NIH Gene Therapy Startup to Increase AAV Gene Therapy EfficiencyWednesday, November 11, 2020
Risk of AAV Mobilization in Gene TherapyMonday, November 9, 2020
Induced Liver Regeneration Enhances CRISPR/Cas9-Mediated Gene RepairThursday, October 8, 2020
Treating Cystic Fibrosis with mRNA Therapy or CRISPRFriday, September 18, 2020
Gene Therapy Corrects the Cardiac Effects of Friedreich’s AtaxiaWednesday, September 2, 2020
Toxicity of Dorsal Root Ganglia Is Widely Associated with CNS AAV Gene Therapy