Human Gene Therapy

Human Gene Therapy Methods

Human Gene Therapy Clinical Development

Editor-in-Chief: Terence R. Flotte, MD
Deputy Editors, Europe: Nathalie Cartier, MD and Thierry VandenDriessche, PhD
Deputy Editors, U.S.: Barry J. Byrne, MD, PhD and Mark A. Kay, MD, PhD
Human Gene Therapy Editor: Guangping Gao, PhD
Methods Editor: Hildegard Büning, PhD
Clinical Development Editor: James M. Wilson, MD, PhD

ISSN: 1043-0342 | Online ISSN: 1557-7422 | Published 22 issues annually | Current Volume: 29

Latest Impact Factor* is 4.241
*2017 Journal Citation Reports® (Clarivate Analytics, 2018)

The definitive rapid-publication journal covering all aspects of gene therapy through original investigations into the transfer and expression of genes in mammals, with in-depth coverage of DNA, RNA, and cell therapies. View Aims & Scope…

Search Subscribe/Renew Recommend This Title Sign Up for TOC Alerts Submit a Paper Share with a Colleague

News Releases

Wednesday, September 19, 2018

Is the End of the Recombinant DNA Advisory Committee (RAC) a Good Thing?

Monday, August 20, 2018

Promising Results Support Continued Development of AAV-Based Human Factor VIII Gene Therapy

Wednesday, August 15, 2018

Longest Reported Efficacy and Safety of AAV5-Based Gene Therapy to Treat Day Blind Sheep with Achromatopsia

Monday, August 13, 2018

Single Injection of Novel Gene Therapy Vector Prolonged Survival in Mouse Model of Pompe Disease

Monday, July 2, 2018

Researchers Show CRISPR Genome Editing Technology Can Correct Alpha-1 Antitrypsin Deficiency

Tuesday, June 12, 2018

Researchers Describe Stem Cell-Derived Organoids for Testing Therapeutic Gene Delivery to Retinal and Photoreceptor Cells

Friday, May 18, 2018

Interview with CAR T Cell Expert Dr. Michel Sadelain in Human Gene Therapy

Tuesday, May 1, 2018

Gene Therapy for Lipoprotein Lipase Deficiency Yields Promising Results

Thursday, April 12, 2018

Genetically Modified Cornea Can Safely and Effectively Prevent Rejection Following Transplantation in High Risk Model

Thursday, March 29, 2018

New Work from Ron Crystal's Lab on Treating Hereditary Adrenal Disorders

The views, opinions, findings, conclusions and recommendations set forth in any Journal article are solely those of the authors of those articles and do not necessarily reflect the views, policy or position of the Journal, its Publisher, its editorial staff or any affiliated Societies and should not be attributed to any of them.