News Releases
Friday, September 18, 2020
Gene Therapy Corrects the Cardiac Effects of Friedreich’s AtaxiaWednesday, September 2, 2020
Toxicity of Dorsal Root Ganglia Is Widely Associated with CNS AAV Gene TherapyThursday, August 13, 2020
Engineered Capsids for Efficient Gene Delivery to the EyeMonday, August 10, 2020
Gene Therapy Targets Inner Retina to Combat BlindnessThursday, March 26, 2020
Benefiting from the National Gene Vector BiorepositoryWednesday, March 18, 2020
Tracking Adeno-Associated Virus Capsid EvolutionTuesday, December 31, 2019
Mayo Clinic Researchers Test Novel Injection of Gene Therapy Vectors Directly into the KidneyTuesday, November 12, 2019
Delivering Large Genes to the Retina is ProblematicFriday, October 25, 2019
Progressing Toward Successful Gene-Based Approaches to Inherited Neurometabolic DiseasesMonday, August 12, 2019
New AAV9 Gene Therapy Vector Dramatically Increases Life Span in Krabbe Disease Mouse Model